News & Publications for:

Timothy Miller

An antisense oligonucleotide against SOD1 delivered intrathecally for patients with SOD1 familial amyotrophic lateral sclerosis: a phase 1, randomised, first-in-man study

Posted on June 3, 2013

Timothy M Miller, Alan Pestronk, William David, Jeff rey Rothstein, Ericka Simpson, Stanley H Appel, Patricia L Andres, Katy Mahoney, Peggy Allred, Katie Alexander, Lyle W Ostrow, David Schoenfeld, Eric A Macklin, Daniel A Norris, Georgios Manousakis, Matthew Crisp, Richard Smith, C Frank Bennett, Kathie M Bishop, Merit E Cudkowicz Read More

Posted in: HPAN, Publications Faculty: ,

Supplementary webappendix

Webappendix

ALS-linked mutant superoxide dismutase 1 (SOD1) alters mitochondrial protein composition and decreases protein import

Posted on October 13, 2010

Li Q, Vande Velde C, Israelson A, Xie J, Bailey AO, Dong MQ, Chun SJ, Roy T, Winer L, Yates JR, Capaldi RA, Cleveland DW, Miller TM (2010). Proc Natl Sci Acad USA, 107(49):21146-51 Read More

Posted in: HPAN, Neurodegeneration, Publications, Therapeutics & Diagnostics Faculty:

Antisense oligonucleotide therapy for neurodegenerative disease

Posted on October 13, 2006

Smith RA, Miller TM, Yamanaka K, Monia BP, Condon TP, Hung G, Lobsiger CS, Ward CM, McAlonis-Downes M, Wei H, Wanceweicz EV, Bennett CF, Cleveland DW (2006). J Clin Invest, 116:2290-2296 Read More

Posted in: HPAN, Neurodegeneration, Publications, Therapeutics & Diagnostics Faculty:

Amyotrophic lateral sclerosis and gene therapy

Posted on October 13, 2006

Miller TM, Smith RA, Cleveland DW (2006). Nat Clin Pract Neurol, 2(9):462-3 Read More

Posted in: HPAN, Neurodegeneration, Publications, Therapeutics & Diagnostics Faculty: